Medicine

Accelerating ASO treatments coming from growth to implementation

.Completing passions.R.S., M.S., H.G. and also A.A.R. are planners of the 1M1M project. H.G. as well as A.A.R. are board of supervisors members as well as R.S., M.S. and A.A.R. are actually members of the clinical advising board of N1C. A.A.R. reveals work by LUMC, which has licenses on exon-skipping technology, a number of which has actually been accredited to BioMarin and also consequently sublicensed to Sarepta. As co-inventor of a number of these patents, A.A.R. was allowed to a share of royalties. A.A.R. further makes known serving as impromptu expert for PTC Rehabs, Sarepta Therapies, Regenxbio, Dyne Rehabs, Lilly, BioMarin Pharmaceuticals Inc., Eisai, Entrada, Takeda, Splicesense, Galapagos, Sapreme, Italfarmaco and Astra Zeneca. Over the last 5 years, A.A.R. likewise conducted speaking to for Alpha Anomeric. A.A.R. likewise mentions membership of the medical boards of advisers of Eisai, Hybridize Therapeutics, Muteness Therapeutics, Sarepta Therapeutics, Sapreme and also Mitorx. Previously 5 years, A.A.R. was actually also a clinical advisory board member for ProQR. Compensation for A.A.R. u00e2 s consulting and suggesting tasks is paid for to LUMC. Before 5 years, LUMC likewise obtained speaker honoraria coming from PTC Therapies, Alnylam Netherlands, Italfarmaco and also Pfizer and also funding for deal analysis coming from Sapreme, Eisai, Galapagos, Synaffix and Alpha Anomeric. Task backing is actually obtained coming from Sarepta Therapies as well as Entrada using unrestricted gives. H.G. has nothing to make known relative to the topics dealt with in this particular composition. Previously 5 years, he has actually additionally obtained consultancy honoraria coming from UCB. M.S. received consultancy honoraria coming from Ionis, UCB, Prevail, Orphazyme, Biogen, Servier, Reata, GenOrph, AviadoBio, Biohaven, Zevra, Lilly and also Solaxa before 5 years, all unrelated to today manuscript. R.S. has nothing to reveal relative to the subject matters covered in this particular composition. She has obtained sound speaker and/or consultancy honoraria or sponsoring additions coming from Abbvie, Bial, STADA as well as Everpharma in the past 5 years.